Ataluren for treating Duchenne muscular dystrophy with a nonsense mutation in the dystrophin gene.
Source: NICE
Date of publication: July, 2016
Publication type: Guidance
In a nutshell: NICE recommends Ataluren for children with Duchenne muscular dystrophy in final guidance.
Some important notes: In case you experience difficulty obtaining this article, please ask your local health librarian to locate this for you.
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